درمان ژنی ۲۰۲۰
Gene Therapy 2020

1. Cover

2. Half Title

3. Title Page

4. Copyright Page

5. Table of Contents

6. Contributors

7. Abbreviations

8. Foreword: Gene therapy — the hype, the reality and the future.

1 Scope and limitations of gene therapy.

2 Tissue-directed gene delivery systems.

3 Retroviral vectors.

4 Adenovirus vectors.

5 Adeno-associated virus vectors for human gene therapy.

6 Liposome delivery systems.

7 Development of mammalian artificial chromosome vectors: prospects for somatic gene transfer.

8 Infectious herpes vectors for gene therapy.

9 Role of animal models in gene therapy.

10 Gene targeting as an approach to gene therapy.

11 Cystic fibrosis.

12 Gene therapy for haemophilia B.

13 Gene therapy for adenosine deaminase deficiency.

14 Cardiovascular disease.

15 Cancer gene therapy I: genetic intervention strategies.

16 Cancer gene therapy II: immunomodulation strategies.

17 The muscular dystrophies.

18 Recent developments in gene therapy for neurological disorders.

27. Index